SMA Daily

🌟 Walking Again: Transforming Lives, One Step at a Time!

FDA Grants Priority Review to Genentech’s Risdiplam for Spinal Muscular Atrophy

Cure SMA to Host a Webinar on Spinraza Access

Spinraza - the First FDA Approved SMA Treatment

Nusinersen Might Become the First Approved SMA Drug

STL-182 Molecule With Therapeutic Potential for Spinal Muscular Atrophy

AveXis Reports Data from Ongoing Phase 1 Trial of Gene Therapy in Spinal Muscular Atrophy Type 1

Exercise May Protect Nerve Cells in Spinal Muscular Atrophy Patients

Discovery of an Enzyme that Plays Critical Role in Spinal Muscular Atrophy

SMA Program Advances with Additional Product Candidate Entering Clinical Development

HSCI researchers find surprising similarities between SMA and ALS

Cytokinteics Presents Results from Phase I Studies of CK-2127107

Russian Scientists Find New Way to Repair DNA that May Cure Spinal Muscular Atrophy

New stem cell research uncovers causes of Spinal Muscular Atrophy

Study on fruit flies and brewer's yeast may provide clues about cause of Spinal Muscular Atrophy

AveXis Gains Orphan Drug Designation from the European Medicines Agency for Gene Therapy Treatment in Spinal Muscular Atrophy

BioBlast Pharma Announces Positive Preclinical for its Read-through Drug Candidate

Data From ISIS-SMN Rx Phase 2 Study in Infants With Spinal Muscular Atrophy Looking Good

Results of Novartis' High Throughput Screening Campaign

PTC Therapeutics Phase 1 Clinical Data on RG7800