AveXis-BioLife Licenses Spinal Muscular Atrophy Gene Therapy Program dne October 24, 2013 AveXis Biolife spinal muscular atrophy spinal muscular atrophy gene therapy spinal muscular atrophy research +
Isis Pharmaceuticals Advances Phase 2 Study of ISIS-SMN Rx in Infants with SMA dne October 04, 2013 clinical trials ISIS Pharmaceuticals ISIS SMNrx spinal muscular atrophy spinal muscular atrophy cure spinal muscular atrophy research +