SMA Program Advances with Additional Product Candidate Entering Clinical Development dne January 10, 2016 PTC Therapeutics RG7800 RG7916 Roche SMA Foundation SMN2 +
BioBlast Pharma Announces Positive Preclinical for its Read-through Drug Candidate dne June 26, 2015 BioBlast Pharma smn protein SMN2 spinal muscular atrophy spinal muscular atrophy cure spinal muscular atrophy research +
Results of Novartis' High Throughput Screening Campaign dne June 10, 2015 Novartis smn protein SMN2 spinal muscular atrophy spinal muscular atrophy cure spinal muscular atrophy research +
PTC Therapeutics Phase 1 Clinical Data on RG7800 dne May 26, 2015 PTC Therapeutics RG7800 Roche SMA Foundation smn protein SMN2 +