AveXis Reports Data from Ongoing Phase 1 Trial of Gene Therapy in Spinal Muscular Atrophy Type 1 dne May 21, 2016 AveXis AVXS-101 spinal muscular atrophy spinal muscular atrophy cure +
Exercise May Protect Nerve Cells in Spinal Muscular Atrophy Patients dne March 25, 2016 physical exercise physical therapy spinal muscular atrophy spinal muscular atrophy research +
Discovery of an Enzyme that Plays Critical Role in Spinal Muscular Atrophy dne February 20, 2016 JNK3 enzyme spinal muscular atrophy spinal muscular atrophy cure spinal muscular atrophy enzyme spinal muscular atrophy research +
SMA Program Advances with Additional Product Candidate Entering Clinical Development dne January 10, 2016 PTC Therapeutics RG7800 RG7916 Roche SMA Foundation SMN2 +
HSCI researchers find surprising similarities between SMA and ALS dne November 28, 2015 ALS amyotrophic lateral sclerosis spinal muscular atrophy spinal muscular atrophy research +