SMA Daily

Cytokinteics Presents Results from Phase I Studies of CK-2127107

Russian Scientists Find New Way to Repair DNA that May Cure Spinal Muscular Atrophy

New stem cell research uncovers causes of Spinal Muscular Atrophy

Study on fruit flies and brewer's yeast may provide clues about cause of Spinal Muscular Atrophy

AveXis Gains Orphan Drug Designation from the European Medicines Agency for Gene Therapy Treatment in Spinal Muscular Atrophy